SEVIN Caroline 

 

Dr. Caroline Sevin is a pediatric neurologist at Kremlin Bicêtre hospital. She leads the French reference center for leukodystrophies in children at Kremlin Bicêtre hospital, France.

 

‪She has  long-standing interests ‬ in neurodegenerative metabolic diseases, including lysosomal, peroxysomal and mitochondrial diseases. She has a strong background in leukodystrophies, particularly ALD, MLD and Krabbe disease. CS is PI or co-PI of several clinical trials, mostly in ALD and MLD, using innovative therapies (gene therapy, intrathecal enzyme replacement therapy, small molecules). Dr Caroline Sevin is member of the ERN-RND and MLDi consortium.

 

She’s member of several DSMBs  for gene therapy trials, and member of the ASGCT, SSIEM, EAN, EPNS. Her research activity focuses on developing in vivo/ex vivo gene therapy approaches for leukodystrophies.‬