PARALLEL SESSION 1 // SMA / NOVEL THERAPIES

4:30 PM • S7L1 • New treatment in Spinal Muscular Atrophy > L. Laurent SERVAIS (Oxford, Uk) 5:00 PM • S7L2 • Improved understanding of SMA and development of further treatment strategies > A. Arthur BURGHES (Columbus Oh, United States) 5:30 PM • S7L3 • Bi-regional newborn screening program for spinal muscular atrophy in France linked to a nationwide strategy for standardized treatment and follow-up > V. Vincent LAUGEL (Strasbourg, France) 5:45 PM • S7L4 • LSD1/PRMT6-targeting gene therapy to attenuate androgen receptor toxic gain-of-function ameliorates SBMA phenotypes in flies and mice. > M. Maria PENNUTO (Padova, Italy)